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Efficacy and safety of vutrisiran for patients with hereditary transthyretin-mediated amyloidosis with polyneuropathy: a randomized clinical trial
16 auth.
D. Adams,
I. Tournev,
Mark S. Taylor,
T. Coelho,
V. Planté-Bordeneuve,
J. Berk,
A. González-Duarte,
J. Gillmore,
S. Low,
Y. Sekijima,
...
L. Obici,
Chongshu Chen,
P. Badri,
S. Arum,
J. Vest,
M. Polydefkis
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7 |
2022 |
7
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🐜
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Probiotics for constipation in Parkinson's disease: A randomized placebo-controlled study.
10 auth.
A. Tan,
Shen-Yang Lim,
Kah Kian Chong,
Mohammad Addin Azhan A Manap,
J. Hor,
Jia Lun Lim,
...
S. Low,
C. Chong,
S. Mahadeva,
A. Lang
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7 |
2020 |
7
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🐜
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Long-term safety and efficacy of patisiran for hereditary transthyretin-mediated amyloidosis with polyneuropathy: 12-month results of an open-label extension study.
425 auth.
David John Adams,
M. Polydefkis,
A. González-Duarte,
J. Wixner,
A. Kristen,
H. Schmidt,
J. Berk,
I. López,
A. Dispenzieri,
D. Quan,
I. Conceição,
M. Slama,
J. Gillmore,
T. Kyriakides,
S. Ajroud-Driss,
...
M. Waddington-Cruz,
M. Mezei,
V. Planté-Bordeneuve,
S. Attarian,
Elizabeth A. Mauricio,
T. Brannagan,
M. Ueda,
E. Aldinc,
Jing Jing Wang,
M. White,
J. Vest,
E. Berber,
M. Sweetser,
T. Coelho,
G. Vita,
V. Rizzo,
M. Russo,
A. Mazzeo,
L. Gentile,
Caitlin Brueckner,
V. Lazzari,
Janice F. Wiesman,
Douglas DeLong,
J. Victory,
J. Dalton,
J. May,
Catherine E. Gilmore,
S. Diallo,
E. Delmont,
J. Pouget,
A. Verschueren,
Aude-Marie Grapperon,
E. Campana-Salort,
A. Lopes,
Filipa Lamas,
Carlos Neves,
J. Castro,
P. Pereira,
I. Castro,
Ana Franco,
M. O. Santos,
C. A. Coutinho,
C. Campos,
A. H. Reis,
Nuno Correia,
J. Pérez,
Ana Martins da Silva,
C. Alves,
Márcio Cardoso,
K. Valdrez,
Júlia R C Monte,
B. Pessoa,
Nádia Guimarães,
Mónica Freitas,
J. Ramalho,
Natália Ferreira,
D. Kuzume,
C. Tard,
N. Waucquier,
I. Rougeaux,
Sylvie Brice,
Emmanuelle Kasprzyk,
E. Elrezzi,
Sayah Meguig,
E. Hachulla,
C. Gauvain,
Maria-Claire Migaud-Chervy,
D. Deplanque,
E. Jozefowicz,
L. Lebellec,
Line Balaya-Gouraya,
Nat LaCour,
Halima Bournane,
N. Martin,
Mongia Elabed,
Niamey Sacko,
Yasmine Boubrit,
Amina Gaouar,
Fetra Rakotondratafika,
M. Théaudin-Saliou,
Cécile Cauquil-Michon,
C. Labeyrie,
A. Not,
A. Al-Salameh,
A. Lecoq,
M. Stéphant,
A. Echaniz-Laguna,
L. Becquemont,
G. Beaudonnet,
V. Algalarrondo,
L. Eliahou,
A. Rousseau,
A. Signaté,
E. Berthelot,
J. Inamo,
Laetitia Vervoitte,
Cécile Focsénéanu,
T. Gendre,
Raphaele Arrouasse,
S. Ayache,
L. Ernande,
P. Corvoisier,
H. Salhi,
A. Choumert,
Vincent Ehinger,
J. Ruíz,
C. Charlin,
Thomas Megelin,
T. Brannagan,
Raisy Fayerman,
Arreum Kim,
A. Paras,
L. J. Gonzalez,
S. Tsang,
Fernanda Wajnsztajn,
Jeffrey Z. Shije,
C. Ulane,
I. Kleyman,
L. Weimer,
Comana Cioroiu,
Sakis Lambrianides,
Rana Abu-Manneh,
E. Zamba-Papanicolaou,
Petros Agathangelou,
Eleni Leonidou,
S. Tada,
A. Fujita,
M. Nagai,
Rina Ando,
Y. Hosokawa,
Y. Yamanishi,
J. Overcash,
E. Giardino,
L. Boyer,
Li Dang,
Andrew Le,
Tyler Nguyen,
Lien Giang,
P. Sellers,
L Tran,
Nghi Truong,
M. Viñas,
Nicole Hrkman,
Sarah Miller,
David Nguyen,
Ashley Smith,
Helen Pu,
Steve Li,
Thao Vuong,
Holly Dioso,
Sinikka Green,
Ki-Ho Lee,
H. Chu,
M. Waters,
Derya Coşkun,
Karla A Zepeda,
W. O'Riordan,
L. Obici,
A. Cortese,
A. Lozza,
G. Merlini,
V. Rosti,
M. Sabatelli,
G. Bisogni,
D. Bernardo,
M. Luigetti,
A. Paolantonio,
V. Guglielmino,
A. Romano,
H. Nienhuis,
J. Bulthuis-Kuiper,
Olga Gerk,
Hannah Ulbricht,
Lenka Taylor,
Eva Meyle,
N. Kleinschmidt,
David Meyrath,
Simone Noe-Schwenn,
U. Meng,
R. Bauer,
F. A. D. Siepen,
Selina Hein,
Tetsuya Takahashi,
Tomohiko Oshita,
Yoko Koujin,
S. Neshige,
T. Nezu,
A. Segawa,
Hiroki Ueno,
H. Morino,
J. Campistol,
Lida María Rodas Marín,
Josep Miquel Blasco Pelicano,
L. G. Dávila,
Marta D. Palacios,
V. Cordoba,
A. G. Sola,
A. Horga,
J. G. Feijoo,
L. P. Isla,
W. Júnior,
M. Moscardini,
Debora Cristina Litcanov,
Ana Flavia Viera Lima,
L. Rodrigues,
Bárbara Marques Coutinho,
C. L. Moreira,
V. D. Marques,
F. Beamud,
Álvaro Gragera Martínez,
C. Borrachero,
E. Barroso,
A. Rodríguez,
M. Sanz,
Elena Rigo Oliver,
J. Moreno,
José M. Martínez,
C. Descals,
Mercedes Usón,
F. J. Vega,
Antoni Figuerola,
C. Montalá,
Moisés Mendes da Silva,
R. Rosa,
L. Pinto,
M. Pinto,
A. Berensztejn,
F. Barroso,
A. Lautre,
Lucas Orellana,
Maria Alejandra González-Duarte Briseño,
K. Cárdenas-Soto,
Brenda Poled Jiménez López,
Sandra Pérez-Castañeda,
C. C. Brito,
D. R. L. Parra,
J. Reyes,
M. D. M. S. Alba,
Elizabeth Mora,
Y. Parman,
Kus Jülide Rezzan,
Erdi Şahin,
N. G. Serbest,
H. Durmuş,
A. Çakar,
Nuriye Ilknur Tugal Tutkun,
S. Karamursel,
A. Elitok,
N. Inan,
Emre Altınkurt,
Jing Ye,
A. C. Allen,
V. Chaudhry,
R. Jarrett,
N. Bressler,
K. Burks,
Qingfeng Liu,
M. Khoshnoodi,
D. Judge,
G. Vista,
S. Shah,
H. Hamaguchi,
J. Oda,
Emiko Fukase,
Ikuko Taniguchi,
Tetsuya Oda,
H. Endo,
Masahiro Shimomura,
Kimitaka Katanazaka,
S. Koto,
T. Nakano,
C. Scheid,
Andreas Zueiter,
L. Pester,
Doreen Walter,
B. Özdemir,
Lukas Frenzel,
U. Holtick,
Jeeyoung Oh,
Hee-Jin Kim,
Hyun Jin Shin,
Kyomin Choi,
T. Yamashita,
T. Masuda,
Y. Misumi,
A. Ueda,
K. Nakahara,
Akiko Yorita,
Seiko Tsuruhisa,
T. Taniwaki,
Masaya Harada,
Taiga Moritaka,
Naonori Sakurada,
Elizabeth A. Mauricio,
Amber Baskin,
E. Dimberg,
A. Fonder,
M. Hobbs,
S. Russell,
Peter M. Dyck,
W. Gonsalves,
N. Leung,
T. Witzig,
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J. Lust,
V. Rajkumar,
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M. Gertz,
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S. Dalia,
E. Carrillo,
P. Gorevic,
Garnette Mason,
C. Chao,
Ming‐Jen Lee,
J. Su,
S. Hsieh,
L. Tsai,
S. Yeh,
Chih-Chao Yang,
S. Ajroud-Driss,
Patricia Casey,
Benjamin C. Joslin,
M. Freimer,
Alison L Sankey,
Amanda Kenepp,
S. Heintzman,
S. Lorusso,
Y. Hokezu,
B. Kim,
Juhyeon Kim,
G. Lee,
E. Cho,
E. Jeon,
J. Min,
J. Seok,
H. Lee,
J. Park,
Y. Sekijima,
Chinatsu Miyazawa,
N. Kato,
D. Kishida,
A. Hineno,
M. Kodaira,
T. Yoshinaga,
Teruyoshi Miyahara,
Akira Imai,
K. Matsumoto,
Kon-Ping Lin,
Yi-Chung Lee,
M. Falk,
B. Pilebro,
O. Suhr,
P. Lindqvist,
K. Soderberg,
F. Pedrosa‐Domellöf,
I. Anan,
E. Nordh,
I. Tournev,
Sashka Zhelyazkova-Glaveeva,
Z. Cherneva,
Staiko Sarafov,
T. Chamova,
Sylvia Cherninkova-Gopina,
Frauke Friebel,
A. Zibert,
N. Mihailovic,
Friederike Schubert,
E. Vorona,
L. Lahme,
Anna Huesing-Kabar,
M. Schilling,
I. Kabar,
A. Martinez-Naharro,
L. Chacko,
O. Cohen,
S. Law,
T. Rezk,
H. Lachmann,
Brianna Blume,
Stacy E. Dixon,
S. Low,
S. Chan,
Hendyono Lim,
K. Goh,
D. Kraus,
Kristin L Jack,
N. Wade,
G. Lopate,
Brittany Zwijack,
J. Florence,
R. Sommerville,
G. Stewart,
J. Ryder,
Linda Mekhael,
Mark Taylor,
Daniel Suan,
Karen Wells,
P. Stone,
Amenze Itoya,
Mercy Owusu-Sekyere,
Desmond Thai,
Ilonah Chahine,
S. Pedrosa,
Thi Hoa Do
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6 |
2020 |
6
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🐢
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Integrating Patient Concerns into Parkinson’s Disease Management
Shen-Yang Lim,
A. Tan,
S. Fox,
A. Evans,
S. Low
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5 |
2017 |
5
🐢
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🐜
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Clinical and genetic profile of patients enrolled in the Transthyretin Amyloidosis Outcomes Survey (THAOS): 14-year update
86 auth.
A. Dispenzieri,
T. Coelho,
I. Conceição,
M. Waddington-Cruz,
J. Wixner,
A. Kristen,
C. Rapezzi,
V. Planté-Bordeneuve,
J. González-Moreno,
M. Maurer,
M. Grogan,
Doug Chapman,
L. Amass,
P. G. Pavía,
Ivaylo Tarnev,
...
J. Costello,
Maria Alejandra González-Duarte Briseño,
H. Schmidt,
B. Drachman,
F. Barroso,
T. Yamashita,
O. Lairez,
Y. Sekijima,
G. Vita,
E. Jeon,
M. Hanna,
D. Slosky,
M. Luigetti,
S. Lorusso,
F. Beamud,
D. Adams,
H. Moelgaard,
R. Press,
C. Cirami,
H. Nienhuis,
J. M. Plana,
J. Inamo,
D. Jacoby,
M. Emdin,
D. Quan,
S. Hummel,
R. Witteles,
A. Dori,
Sanjiv Shah,
D. Lenihan,
O. Azevedo,
S. Murali,
S. Živković,
S. Low,
J. Nativi-Nicolau,
N. Fine,
J. Tallaj,
C. Tschoepe,
R. Torrón,
M. Polydefkis,
G. Merlini,
S. Bădeliță,
Stephen S. Gottlieb,
J. Tauras,
E. B. Correia,
H. Ventura,
B. Gess,
F. Darstein,
Jeeyoung Oh,
Tessa Marburger,
J. Van Cleemput,
V. Salutto,
Y. Parman,
C. Chao,
N. Sarswat,
Christopher Mueller,
D. Steidley,
J. Ralph,
A. Warner,
W. Cotts,
J. Hoffman,
M. Rugiero,
S. Misawa,
J. L. Blanco,
L. G. Dávila,
M. Sadeh,
Jinju Luo,
T. Kyriakides,
Annabel K. Wang,
H. Kaufmann,
S. Živković
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5 |
2022 |
5
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🐜
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Probiotics for Constipation in Parkinson Disease
10 auth.
A. Tan,
Shen-Yang Lim,
Kah Kian Chong,
Mohammad Addin Azhan A Manap,
J. Hor,
Jia Lun Lim,
...
S. Low,
C. Chong,
S. Mahadeva,
A. Lang
|
4 |
2021 |
4
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|
🐜
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Characteristics of Patients with Late- vs. Early-Onset Val30Met Transthyretin Amyloidosis from the Transthyretin Amyloidosis Outcomes Survey (THAOS)
43 auth.
M. Waddington-Cruz,
J. Wixner,
L. Amass,
Jan Kiszko,
Doug Chapman,
Y. Ando,
F. Barroso,
M. Rugiero,
J. Van Cleemput,
Ivaylo Tarnev,
T. Kyriakides,
A. Kristen,
H. Schmidt,
F. Darstein,
B. Gess,
...
J. M. Plana,
J. Moreno,
J. Costello,
P. G. Pavía,
R. Torrón,
F. Beamud,
V. Planté-Bordeneuve,
D. Adams,
O. Lairez,
C. Rapezzi,
G. Merlini,
M. Luigetti,
Y. Sekijima,
T. Yamashita,
S. Misawa,
S. Low,
H. Nienhuis,
T. Coelho,
I. Conceição,
R. Press,
Y. Parman,
M. Maurer,
S. Gottlieb,
Annabel K. Wang,
B. Drachman,
A. Dispenzieri,
S. Živković,
D. Lenihan
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4 |
2021 |
4
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🦁
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Ala97Ser mutation is common among ethnic Chinese Malaysians with transthyretin familial amyloid polyneuropathy
9 auth.
S. Low,
Cheng-Yin Tan,
Nor Ashikin Md Sari,
A. Ahmad-Annuar,
K. Wong,
Kon-Ping Lin,
...
N. Shahrizaila,
C. Tan,
K. Goh
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3 |
2019 |
3
🦁
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|
🐜
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Impact of Vutrisiran on Quality of Life and Physical Function in Patients with Hereditary Transthyretin-Mediated Amyloidosis with Polyneuropathy
341 auth.
L. Obici,
S. Ajroud-Driss,
Kon-Ping Lin,
J. Berk,
J. Gillmore,
P. Kale,
H. Koike,
D. Danese,
E. Aldinc,
Chongshu Chen,
J. Vest,
D. Adams,
J. Wixner,
Rolf Backlund,
B. Pilebro,
...
I. Anan,
F. Edbom,
A. Ekman,
S. Arvidsson,
Ulrika Englund,
Karin Söderberg,
E. Nordh,
Erica Unéus,
K. Samuelsson,
Anna Nilzen,
R. Press,
Mirjam Bilecen,
T. Coelho,
M. Novais,
P. Rodrigues,
Ana Martins da Silva,
I. Cardoso,
C. Rodrigues,
J. Ramalho,
H. Martins,
Mónica Silva,
Nádia Guimarães,
J. Pérez,
A. H. Reis,
Júlia R C Monte,
Natália Ferreira,
C. Alves,
Márcio Cardoso,
R. Teixeira,
I. Conceição,
Filipa Lamas,
M. Oliveira Santos,
C. Campos,
Conceiçao de Azevedo Coutinho,
J. Castro,
I. Castro,
D. Silva,
S. Gonçalves,
Eleonora Di Buduo,
Claudia Sforzini,
R. Mussinelli,
V. Rosti,
A. Lozza,
Anna Racchi,
M. Sabatelli,
M. Luigetti,
G. Bisogni,
A. Romano,
V. Guglielmino,
A. Di Paolantonio,
D. Bernardo,
G. Vita,
A. Mazzeo,
M. Russo,
D. Pareyson,
D. Calabrese,
S. Fenu,
P. Saveri,
H. Nienhuis,
G. Bokhorst,
Carlien Roos,
M. Couperus,
Greetje De Jong,
A. Brunger,
G. Drost,
F. Lange,
Adinda Colauto,
M. Waddington-Cruz,
A. Abreu,
R. Pedrosa,
Renata Gervais de Santa Rosa,
Moises Dias,
Fetra Rakotondratafika,
A. Echaniz-Laguna,
C. Cauquil,
C. Labeyrie,
G. Beaudonnet,
Yasmine Boubrit,
Amina Gaouar,
H. Bourenane,
S. Attarian,
Elsaid Yahia,
A. Verschueren,
Aude-Marie Grapperon,
E. Delmont,
V. Planté-Bordeneuve,
Laetitia Vervoitte,
S. Ayache,
P. Le Corvoisier,
Raphaele Arrouasse,
T. Gendre,
L. Abou Chakra,
Cécile Focsénéanu,
C. Barau,
G. Solé,
Laurie Belin,
M. Violleau,
Fanny Duval-Bontemps,
R. Massie,
Xin Dong,
F. Muñoz-Beamud,
Sandra García Garrido,
C. Borrachero,
Alvaro Gragera Martinez,
L. Galán Dávila,
Marta Palacios,
Laura Vicente,
L. Pérez de Isla,
C. Casasnovas,
Carles Diez Lopez,
E. Fabra,
J. González-Costello,
Sonia Guerrero,
S. Yun Viladomat,
Yurema Martinez,
Valentina Vélez-Santamaría,
Velina Nedkova-Hristova,
P. García Pavía,
Ariadna Gonzalez Segovia,
F. de Frutos,
E. Gonzalez-Lopez,
F. Domínguez,
Luis Escobar-Lopez,
Eva Cabrera-Romero,
Paula Sánchez Gismera,
María de la Iglesia,
F. Martinez Valle,
Gonzalo Mazuela Aguila,
Karen Lorite,
N. Raguer,
P. Suñé,
Pablo Piera,
Carlos Ortega,
Carolina Aguilar,
Gisela Gili,
H. Schmidt,
Christel Langenstroer,
A. Hüsing-Kabar,
I. Kabar,
Matthias Schilling,
Frauke Friebel,
Phil Tepasse,
F. Birklein,
Monika Firros,
F. Escolano-Lozano,
Caitlin Brueckner,
Vanessa Bahnam,
M. Kaku,
K. Lau,
Janice F. Wiesman,
M. Grogan,
Susannah Miller,
J. Frantz,
D. C. Schmidt,
Omar F. AbouEzzeddine,
Wayne I. Miller,
Grace Lin,
M. Gertz,
A. Dispenzieri,
T. Brannagan,
Raisy Fayerman,
Elizabeth DuVerger,
J. Cabrera,
M. Maurer,
C. Ulane,
L. Weimer,
S. Tsang,
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Nathan Carberry,
Sai Si Thu,
D. Quan,
Brianna Blume,
J. Overcash,
He Pu,
Ki-Ho Lee,
H. Chu,
Karla P. Zepeda,
M. Waters,
Thao Vuong,
Derya Coşkun,
Kim J. Quillin,
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M. Polydefkis,
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G. Vista,
Tae Hwan Chung,
Michele Watt,
Daniel Tsottles,
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Dayna Carlson,
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M. Shanks,
Karen Maslowski,
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Florencia Picone,
A. Lautre,
Lucas Orellana,
Wenqin Du,
J. Felius,
A. González-Duarte,
Karla Cardenas Soto,
Rebecca E. Traub,
M. Chopra,
C. Chao,
Chia-Hua Hsu,
Li-Kai Tsai,
Ming‐Jen Lee,
J. Su,
S. Hsieh,
Hsueh-Wen Hsueh,
Hsi-Chieh Chou,
Byoung-Joon Kim,
Hyesun Kang,
J. Min,
E. Jeon,
Yeon Hak Chung,
J. Park,
Jeeyoung Oh,
Hyung Joo Jeong,
I. Tournev,
S. Zhelyazkova,
Y. Misumi,
Y. Sakamoto,
Nami Hashimoto,
Yoshimi Misumi,
A. Takahashi,
M. Ueda,
T. Masuda,
A. Ueda,
M. Katsuno,
Kazuki Tajima,
Momoko Sumi,
Fujiko Hasegawa,
T. Okumura,
M. Iijima,
Y. Fukami,
D. Ito,
Yoshiyuki Kishimoto,
Tomoyuki Kazuta,
Katsuhiko Kato,
N. Mouri,
S. Furukawa,
R. Nishi,
Y. Sekijima,
Keiko Ito,
Naga-aki Kato,
D. Kishida,
H. Mochizuki,
Kaori Okada,
Kurumi Ohashi,
K. Ikenaka,
M. Nakamori,
Makoto Kinoshita,
B. R. Mapalo,
S. Law,
L. Chacko,
H. Lachmann,
O. Cohen,
Y. Razvi,
S. Varughese,
A. Martinez-Naharro,
R. Orrell,
M. Fontana,
L. Rannigan,
Sarah Louth,
E. Zamba-Papanicolaou,
Demetra Charalamnibous,
Rana Abu Manneh,
K. Kleopa,
T. Christodoulides,
S. Frangos,
M. Galganski-Cleanthous,
E. Gaglia,
Irene Smoleski,
E. Kkolou,
Andry Ploutarchou,
Mariana Hanghiuc,
Galini Chroidou,
Olga Stylianou,
Anastasia Krokou,
Irene Zannetou,
E. Kastritis,
D. Papadopoulou,
Ilias Spinasas,
Panayiotis Bakalis,
N. Kanellias,
D. Fotiou,
I. Dialoupi,
Magdalini Migko,
M. Gavriatopoulou,
S. Low,
Mark S. Taylor,
G. Stewart,
H. Knight,
S. Vucic,
Antonia S Carroll,
Matthew Silsby,
Daniel Suan,
S. Gibbs,
Carmela Corfield,
Suzana Jakicic,
Hayden Jina,
S. Ting,
S. Q. Wong,
P. Mollee,
L. McKinley,
E. Abro,
D. Korczyk,
G. Remiche,
N. Alaerts,
Fabienne De Veylder,
K. Claeys,
Elisa Debien,
Joyce Cremers,
A. D'Hondt,
Bram De Wel
|
3 |
2023 |
3
🐜
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