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Systemic restoration of UBA1 ameliorates disease in spinal muscular atrophy
16 auth.
Rachael A. Powis,
Evangelia Karyka,
Penelope Boyd,
Julien Côme,
Ross A. Jones,
Yinan Zheng,
Eva Szunyogová,
E. Groen,
Gillian Hunter,
Derek Thomson,
...
T. Wishart,
Catherina G. Becker,
S. Parson,
Cécile Martinat,
M. Azzouz,
T. Gillingwater
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7 |
2016 |
7 🐜
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