π
|
Long-Term Engraftment and Fetal Globin Induction upon BCL11A Gene Editing in Bone-Marrow-Derived CD34+ Hematopoietic Stem and Progenitor Cells
20 auth.
KaiβHsin Chang,
Sarah Smith,
T. Sullivan,
Kai Chen,
Qianhe Zhou,
J. West,
Mei Liu,
Yingchun Liu,
B. Vieira,
Chao Sun,
...
Vu P. Hong,
Mingxuan Zhang,
X. Yang,
A. Reik,
F. Urnov,
E. Rebar,
M. Holmes,
O. Danos,
Haiyan Jiang,
Siyuan Tan
|
7 |
2017 |
7 π
|
π
|
A whole-genome sequence study identifies genetic risk factors for neuromyelitis optica
13 auth.
K. Estrada,
Christopher W. Whelan,
Fengmei Zhao,
P. Bronson,
R. Handsaker,
Chao Sun,
J. Carulli,
Tim Harris,
R. Ransohoff,
S. Mccarroll,
...
A. Day-Williams,
B. Greenberg,
D. MacArthur
|
6 |
2018 |
6 π
|
π
|
Newborn blood spot screening test using multiplexed real-time PCR to simultaneously screen for spinal muscular atrophy and severe combined immunodeficiency.
10 auth.
Jennifer L Taylor,
F. Lee,
G. Yazdanpanah,
J. Staropoli,
Mei Liu,
J. Carulli,
...
Chao Sun,
S. Dobrowolski,
W. H. Hannon,
R. Vogt
|
6 |
2015 |
6 π
|
π
|
Parkinsonβs disease associated with pure ATXN10 repeat expansion
14 auth.
B. SchΓΌle,
K. McFarland,
Kelsey Lee,
Y. Tsai,
Khanh-dung Nguyen,
Chao Sun,
Mei Liu,
Christie Byrne,
Ramesh Gopi,
Neng Huang,
...
J. Langston,
Tyson A. Clark,
Francisco Javier JimΓ©nez Gil,
T. Ashizawa
|
5 |
2017 |
5 π
|
π
|
Longitudinal analysis of peripheral blood T cell receptor diversity in patients with systemic lupus erythematosus by next-generation sequencing
9 auth.
D. Thapa,
Raffi Tonikian,
Chao Sun,
Mei Liu,
Andrea Dearth,
M. Petri,
...
F. PΓ©pin,
R. Emerson,
A. Ranger
|
5 |
2015 |
5 π
|
π¦
|
Peptidoglycan recognition proteins Pglyrp3 and Pglyrp4 are encoded from the epidermal differentiation complex and are candidate genes for the Psors4 locus on chromosome 1q21
9 auth.
Chao Sun,
P. Mathur,
J. Dupuis,
R. Tizard,
B. Ticho,
T. Crowell,
...
H. Gardner,
A. Bowcock,
J. Carulli
|
5 |
2006 |
5 π¦
|
π
|
Organotypic Brain Slice Culture Microglia Exhibit Molecular Similarity to Acutely-Isolated Adult Microglia and Provide a Platform to Study Neuroinflammation
19 auth.
A. R. D. Delbridge,
Dann Huh,
M. Brickelmaier,
J. Burns,
C. Roberts,
Ravi Challa,
N. Raymond,
P. Cullen,
Thomas M. Carlile,
K. Ennis,
...
Mei Liu,
Chao Sun,
N. Allaire,
M. Foos,
Hui-hsin Tsai,
N. Franchimont,
R. Ransohoff,
C. Butts,
M. Mingueneau
|
5 |
2020 |
5 π
|
π¦
|
Kirrel2, a novel immunoglobulin superfamily gene expressed primarily in beta cells of the pancreatic islets.
8 auth.
Chao Sun,
D. Kilburn,
A. Lukashin,
T. Crowell,
H. Gardner,
R. Brundiers,
...
B. Diefenbach,
J. Carulli
|
5 |
2003 |
5 π¦
|
π
|
Highly efficient neuronal gene knockout in vivo by CRISPR-Cas9 via neonatal intracerebroventricular injection of AAV in mice
15 auth.
S. Hana,
Michael Peterson,
Helen McLaughlin,
Eric Marshall,
A. Fabian,
Olivia McKissick,
Kathryn Koszka,
Galina Marsh,
M. Craft,
Shanqin Xu,
...
Alexander G. Sorets,
Tess Torregrosa,
Chao Sun,
C. E. Henderson,
S. Lo
|
5 |
2021 |
5 π
|