BetterScholar BetterScholar
8
Role
Title
Level Year L/R
🐜 Onasemnogene abeparvovec gene therapy for symptomatic infantile-onset spinal muscular atrophy type 1 (STR1VE-EU): an open-label, single-arm, multicentre, phase 3 trial
55 auth. E. Mercuri, F. Muntoni, G. Baranello, R. Masson, O. Boespflug-Tanguy, Claudio Bruno, S. Corti, A. Daron, N. Deconinck, L. Servais, V. Straub, H. Ouyang, D. Chand, S. Tauscher‐Wisniewski, N. Mendonça, ... A. Lavrov, A. Seferian, S. Lucia, S. Tachibana, A. Jollet, S. Mouffak, M. Pedemonte, N. Brolatti, S. Morando, A. Vanlander, E. D. Vos, V. Tahon, A. Govoni, F. Magri, G. Comi, M. Foa, V. Parente, L. Buscemi, F. Farra, O. Schneider, A. Jonas, A. Defeldre, E. Pagliano, R. Zanin, M. Arnoldi, V. Schembri, M. Sole, A. Mandelli, M. Pera, L. Antonaci, G. Coratti, R. D. Sanctis, M. Pane, M. Scoto, K. Groves, L. Edel, F. Abel, H. V. Ruiten, R. M. Lofra, E. Thompson
7 2021
7
🐜
🦁 Why are some patients with Duchenne muscular dystrophy dying young: An analysis of causes of death in North East England.
9 auth. H. V. Ruiten, H. V. Ruiten, C. Bettolo, Tim Cheetham, M. Eagle, Hanns Lochmüller, ... Volker Straub, K. Bushby, M. Guglieri
6 2016
6
🦁
🦁 Why are some patients with Duchenne muscular dystrophy dying young: An analysis of causes of death in North East England.
9 auth. H. V. Ruiten, H. V. Ruiten, C. Bettolo, Tim Cheetham, M. Eagle, Hanns Lochmüller, ... Volker Straub, K. Bushby, M. Guglieri
6 2016
6
🦁
🐜 Alveolar PCO2 oscillations and ventilation at sea level and at high altitude.
8 auth. D. Collier, A. Nickol, J. Milledge, H. V. Ruiten, C. Collier, E. Swenson, ... A. Datta, C. Wolff
3 2008
3
🐜
🐬 G.P.161 Improving the diagnosis of Duchenne muscular dystrophy
M. Guglieri, H. V. Ruiten, V. Straub, K. Bushby
1 2014
1
🐬
🐬 G.P.45 Cautionary tale in Duchenne muscular dystrophy – Opioids in neuromuscular disorders
C. Bettolo, M. Guglieri, H. V. Ruiten, V. Straub, Hanns Lochmüller
0 2015
0
🐬
🦁 Impact of three decades of improvements in standards of care on clinical outcomes in Duchenne muscular dystrophy
10 auth. H. V. Ruiten, Aura Cecilia Jimenez-Moreno, E. Elliot, A. Mayhew, M. James, C. Marini-Bettolo, ... Hanns Lochmüller, V. Straub, K. Bushby, M. Guglieri
0 2017
0
🦁
🐬 449 Improving the care of neurosurgical patients: a new teaching model for paediatric trainees
Chris Angus, H. V. Ruiten, Albert Lim, I. Coulter
0 2023
0
🐬