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Real-world multidisciplinary outcomes of onasemnogene abeparvovec monotherapy in patients with spinal muscular atrophy type 1: experience of the French cohort in the first three years of treatment
29 auth.
I. Desguerre,
R. Barrois,
F. Audic,
C. Barnerias,
Brigitte Chabrol,
Jean-Baptiste Davion,
J. Durigneux,
C. Espil‐Taris,
Marta Gómez-García de la Banda,
Marine Guichard,
Arnaud Isapof,
Marie-Christine Nouguès,
Vincent Laugel,
Laure Le Goff,
Sandra Mercier,
...
Anne Pervillé,
Christian Richelme,
Marie Thibaud,
C. Sarret,
Cyril Schweitzer,
Hervé Testard,
V. Trommsdorff,
C. Vanhulle,
U. Walther-Louvier,
C. Altuzarra,
M. Chouchane,
J. Ropars,
Susana Quijano-Roy,
C. Cances
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1 |
2024 |
1
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