π
|
Apilimod dimesylate in C9orf72 amyotrophic lateral sclerosis: a randomized phase 2a clinical trial.
18 auth.
Suma Babu,
Katharine A. Nicholson,
Jeffrey D. Rothstein,
Andrea Swenson,
Paul J Sampognaro,
Pravin Pant,
Eric Macklin,
Susan Spruill,
Sabrina Paganoni,
Tania F. Gendron,
...
M. Prudencio,
Leonard Petrucelli,
Darrell Nix,
Sean Landrette,
Esther Nkrumah,
Keith Fandrick,
Joan Edwards,
Peter R Young
|
2 |
2024 |
2 π
|
π
|
CNM-Au8 in Amyotrophic Lateral Sclerosis: The HEALEY ALS Platform Trial.
90 auth.
James D. Berry,
N. Maragakis,
Eric A Macklin,
Lori B. Chibnik,
Melanie Quintana,
Benjamin R. Saville,
M. Detry,
Matteo Vestrucci,
Joe Marion,
A. McGlothlin,
Elijah W. Stommel,
Marianne K. Chase,
Lindsay Pothier,
Brittney A. Harkey,
Hong Yu,
...
Alexander V. Sherman,
Jeremy M Shefner,
Meghan Hall,
Gale Kittle,
Suma Babu,
Jinsy Andrews,
Derek DβAgostino,
Eric Tustison,
Erica Scirocco,
Elisa Giacomelli,
Gustavo Alameda,
Eduardo Locatelli,
Doreen T Ho,
Adam Quick,
S. Ajroud-Driss,
Jonathan Katz,
D. Heitzman,
Stanley H. Appel,
S. Shroff,
Kevin J. Felice,
Z. Simmons,
Timothy M. Miller,
Nicholas Olney,
Michael D Weiss,
Stephen A. Goutman,
J. A. Fernandes,
O. Jawdat,
M. Owegi,
Laura Foster,
Tuan Vu,
H. Ilieva,
Daniel S. Newman,
Ximena Arcila-Londono,
Carlayne E. Jackson,
S. Ladha,
T. Heiman-Patterson,
J. Caress,
Andrea Swenson,
Amanda Peltier,
Richard Lewis,
Dominic Fee,
Matthew Elliott,
Richard S Bedlack,
E. Kasarskis,
Lauren Elman,
Jeffrey Rosenfeld,
David Walk,
Courtney E. Mcilduff,
Paul Twydell,
Eufrosina Young,
Kristin Johnson,
K. Rezania,
Namita A Goyal,
Jeffrey A. Cohen,
Michael Benatar,
Vovanti Jones,
Jonathan D. Glass,
Jaimin Shah,
S. Beydoun,
J. Wymer,
Lindsay Zilliox,
Shakti Nayar,
Gary L. Pattee,
Jennifer M. Martinez-Thompson,
Austin Rynders,
Jacob Evan,
Jeremy Evan,
Alan Hartford,
Marjan Sepassi,
Karen S. Ho,
R. Glanzman,
Benjamin Greenberg,
M. Hotchkin,
Sabrina Paganoni,
M. Cudkowicz
|
1 |
2025 |
1 π
|
π
|
Efficacy and Safety of Zilucoplan in Amyotrophic Lateral Sclerosis
85 auth.
Sabrina Paganoni,
Christina N. Fournier,
Eric A Macklin,
Lori B. Chibnik,
Melanie Quintana,
Benjamin R. Saville,
M. Detry,
Matteo Vestrucci,
Joe Marion,
A. McGlothlin,
S. Ajroud-Driss,
Marianne K. Chase,
Lindsay Pothier,
Brittney A. Harkey,
Hong Yu,
...
Alexander V. Sherman,
J. Shefner,
Meghan Hall,
Gale Kittle,
James D. Berry,
Suma Babu,
Jinsy Andrews,
Derek Dagostino,
Eric Tustison,
Elisa Giacomelli,
Erica Scirocco,
Gustavo Alameda,
Eduardo Locatelli,
Doreen T Ho,
Adam Quick,
Jonathan Katz,
D. Heitzman,
Stanley H. Appel,
S. Shroff,
Kevin J. Felice,
N. Maragakis,
Z. Simmons,
Timothy M. Miller,
Nicholas Olney,
Michael D Weiss,
Stephen A. Goutman,
J. A. Fernandes,
O. Jawdat,
M. Owegi,
Laura Foster,
Tuan Vu,
H. Ilieva,
Daniel S. Newman,
Ximena Arcila-Londono,
Carlayne E. Jackson,
S. Ladha,
T. Heiman-Patterson,
J. Caress,
Andrea Swenson,
Amanda Peltier,
Richard Lewis,
Dominic Fee,
Matthew Elliott,
Richard S Bedlack,
E. Kasarskis,
Lauren Elman,
Jeffrey Rosenfeld,
David Walk,
Courtney E. Mcilduff,
Paul Twydell,
Eufrosina Young,
Kristin Johnson,
K. Rezania,
Namita A Goyal,
Jeffrey A. Cohen,
Michael Benatar,
Vovanti Jones,
Jonathan D. Glass,
Jaimin S. Shah,
S. Beydoun,
J. Wymer,
Lindsay Zilliox,
Shakti Nayar,
Gary L. Pattee,
Jennifer M. Martinez-Thompson,
Brittany Harvey,
Shital Patel,
Paul Mahoney,
P. Duda,
M. Cudkowicz
|
0 |
2025 |
0 π
|