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Long-term safety and efficacy of elexacaftor/tezacaftor/ivacaftor in people with cystic fibrosis and at least one F508del allele: 144-week interim results from a 192-week open-label extension study
23 auth.
C. Daines,
Elizabeth Tullis,
Stefano Costa,
Rachel W. Linnemann,
M. A. Mall,
E. McKone,
Deepika Polineni,
B. Quon,
F. C. Ringshausen,
Steven M. Rowe,
...
H. Selvadurai,
J. Taylor-Cousar,
Nicholas J. Withers,
N. Ahluwalia,
Samuel M. Moskowitz,
Valentin Prieto-Centurion,
Yaoyuan Vincent Tan,
S. Tian,
T. Weinstock,
Fengjuan Xuan,
Yaohua Zhang,
Bonnie Ramsey,
Matthias Griese
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5 |
2023 |
5 🐜
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🐢
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Airway clearance management in people with bronchiectasis: data from the European Bronchiectasis Registry (EMBARC)
38 auth.
A. Spinou,
Beatriz Hererro-Cortina,
S. Aliberti,
P. Goeminne,
E. Polverino,
K. Dimakou,
C. Haworth,
Michael R. Loebinger,
A. De Soyza,
M. Vendrell,
Pierre-Régis Burgel,
M. McDonnell,
S. Sutharsan,
Sabina Škrgat,
Luiz Maiz-Carro,
...
O. Sibila,
D. Stolz,
P. Kauppi,
A. Bossios,
A. Hill,
Ian Clifton,
M. Crichton,
Paul Walker,
R. Menéndez,
Sermin Borecki,
Dušanka Obradović,
A. Nowiński,
A. Amorim,
Antoní Torres,
N. Lorent,
Tobias Welte,
Francesco Blasi,
M. Janković Makek,
M. Shteinberg,
W. Boersma,
J. Elborn,
James D. Chalmers,
F. C. Ringshausen
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4 |
2024 |
4 🐢
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Analyses of 1236 genotyped primary ciliary dyskinesia individuals identify regional clusters of distinct DNA variants and significant genotype–phenotype correlations
66 auth.
J. Raidt,
Sarah Riepenhausen,
P. Pennekamp,
H. Olbrich,
I. Amirav,
R. Athanazio,
M. Aviram,
J. Balinotti,
Ophir Bar-On,
Sebastian Fn Bode,
Mieke Boon,
M. Borrelli,
SB Carr,
Suzanne Crowley,
Eleonora Dehlink,
...
Sandra Diepenhorst,
P. Ďurdík,
Bernd Dworniczak,
N. Emiralioğlu,
Ela Erdem,
Rossella Fonnesu,
Serena Gracci,
J. Große-Onnebrink,
Karolina Gwozdziewicz,
E. Haarman,
Christine R Hansen,
Clare Hogg,
M. Holgersen,
E. Kerem,
R. W. Körner,
K. Kötz,
Panayiotis Kouis,
MR Loebinger,
N. Lorent,
Jane S Lucas,
Debora Maj,
M. A. Mall,
J. Marthin,
V. Martinů,
Henryk Mazurek,
Hannah M. Mitchison,
T. Nöthe-Menchen,
U. Özçeli̇k,
Massimo Pifferi,
A. Pogorzelski,
F. C. Ringshausen,
J. Roehmel,
S. Rovira-Amigo,
Nisreen Rumman,
A. Schlegtendal,
A. Shoemark,
Synne Sperstad Kennelly,
Ben O Staar,
S. Sutharsan,
Simon Thomas,
Nicola Ullmann,
Julian Varghese,
Sandra von Hardenberg,
W. Walker,
M. Wetzke,
M. Witt,
P. Yiallouros,
A. Zschocke,
E. Ziętkiewicz,
Kim G Nielsen,
H. Omran
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3 |
2024 |
3 🐜
|
🐜
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Objective sputum colour assessment and clinical outcomes in bronchiectasis: data from the European Bronchiectasis Registry (EMBARC)
41 auth.
S. Aliberti,
F. C. Ringshausen,
Raja Dhar,
C. Haworth,
Michael R. Loebinger,
K. Dimakou,
M. Crichton,
A. De Soyza,
M. Vendrell,
Pierre-Régis Burgel,
M. McDonnell,
Sabina Škrgat,
Luis Maiz Carro,
A. de Roux,
O. Sibila,
...
A. Bossios,
M. M. van der Eerden,
P. Kauppi,
Robert Wilson,
Branislava Milenković,
R. Menéndez,
Marlène S. Murris,
S. Borekci,
O. Munteanu,
Dušanka Obradović,
A. Nowiński,
A. Amorim,
Antoní Torres,
N. Lorent,
E. Van Braeckel,
J. Altenburg,
A. Shoemark,
M. Shteinberg,
W. Boersma,
P. Goeminne,
J. Elborn,
A. Hill,
Tobias Welte,
Francesco Blasi,
E. Polverino,
James D. Chalmers
|
3 |
2024 |
3 🐜
|
🐜
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PREFUL MRI for Monitoring Perfusion and Ventilation Changes after Elexacaftor-Tezacaftor-Ivacaftor Therapy for Cystic Fibrosis: A Feasibility Study.
12 auth.
M. Dohna,
A. Voskrebenzev,
F. Klimeš,
Till F Kaireit,
Julian Glandorf,
S. Pallenberg,
...
F. C. Ringshausen,
Gesine Hansen,
D. M. Renz,
Frank Wacker,
Anna-Maria Dittrich,
Jens Vogel-Claussen
|
3 |
2024 |
3 🐜
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🐜
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Primary Ciliary Dyskinesia in Adult Bronchiectasis
60 auth.
Raphael Ewen,
Isabell Pink,
S. Sutharsan,
Sven P. Aries,
A. Grünewaldt,
Amelia Shoemark,
U. Sommerwerck,
Ben O Staar,
Sabine Wege,
Pontus Mertsch,
J. Rademacher,
F. C. Ringshausen,
Borghild Bad Stefan Katarina Andrés de Ralf Hartmut Christi Grün Windsheim Dargel Ludwig Roux Otto-Knapp Lode ,
Borghild Grün,
Bad Windsheim,
...
Stefan Dargel,
Katarina Ludwig,
A. Roux,
Ralf Otto-Knapp,
Hartmut Lode,
Christian Gogoll,
Meike Probst,
Frank Herrmann,
Axel Overlack,
Stefan Pabst,
U. Sommerwerck,
K. H. Vehar,
Stefan Blaas,
Bernhard Schaaf,
M. Kolditz,
S. Sutharsan,
Essen; Peter Kardos,
A. Grünewaldt,
Stephan Sorichter,
Tobias Scholz,
Marco Idzko,
Moritz Mohadjer,
Stephan Eisenmann,
Sven P. Aries,
Johannes Lauer-Hermfisse,
Sabine Kampf,
F. C. Ringshausen,
Sabine Wege,
F. Herth,
S. Ewig,
Christian Reinhardt,
S. Andreas,
Christian Schumann,
Ingrid Bobis,
Thomas Bahmer,
Kiel; Rita Fey,
Martin Jüch,
Lostau; Axel T. Kempa,
Erika Piirsoo,
B. Klapdor,
Pontus Mertsch,
Bernhard Schmidt,
Holger Hein,
P. Haidl,
Jorge Fernando Gamarra
|
2 |
2024 |
2 🐜
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