🐜
|
TDP-43 loss and ALS-risk SNPs drive mis-splicing and depletion of UNC13A
97 auth.
Anna L. Brown,
O. Wilkins,
M. Keuss,
Sarah E. Hill,
M. Zanovello,
Weaverly Colleen Lee,
A. Bampton,
Flora C. Y. Lee,
L. Masino,
Y. Qi,
S. Bryce-Smith,
A. Gatt,
Martina Hallegger,
D. Fagegaltier,
H. Phatnani,
...
Justin Kwan,
D. Sareen,
James R. Broach,
Zachary Simmons,
Ximena Arcila-Londono,
Edward B. Lee,
V. V. Van Deerlin,
N. Shneider,
E. Fraenkel,
L. Ostrow,
Frank Baas,
Noah Zaitlen,
James D. Berry,
A. Malaspina,
P. Fratta,
Gregory A. Cox,
Leslie M. Thompson,
Steve Finkbeiner,
E. Dardiotis,
Timothy Miller,
Siddharthan Chandran,
S. Pal,
E. Hornstein,
D. Macgowan,
T. Heiman-Patterson,
M. G. Hammell,
N. Patsopoulos,
O. Butovsky,
Joshua Dubnau,
Avindra Nath,
Robert Bowser,
Matthew M Harms,
Eleonora Aronica,
Mary Poss,
Jennifer Phillips-Cremins,
John Crary,
N. Atassi,
Dale J. Lange,
Darius J. Adams,
Leonidas Stefanis,
M. Gotkine,
Robert H. Baloh,
Suma Babu,
T. Raj,
S. Paganoni,
Ophir Shalem,
Colin Smith,
Bin Zhang,
Brent Harris,
Iris J. Broce,
V. Drory,
J. Ravits,
Corey McMillan,
Vilas Menon,
Lani Wu,
Steve Altschuler,
Y. Lerner,
Rita Sattler,
K. Van Keuren-Jensen,
O. Rozenblatt-Rosen,
Kerstin Lindblad-Toh,
Katharine Nicholson,
Peter Gregersen,
J. Lee,
Sulev Kokos,
Stephen Muljo,
J. Newcombe,
E. Gustavsson,
S. Seddighi,
Joel F Reyes,
Steve Coon,
Daniel M. Ramos,
G. Schiavo,
E.M.C. Fisher,
T. Raj,
M. Secrier,
T. Lashley,
J. Ule,
E. Buratti,
J. Humphrey,
Michael E. Ward,
P. Fratta
|
7 |
2022 |
7 🐜
|
🐜
|
The cycad genotoxin methylazoxymethanol, linked to Guam ALS/PDC, induces transcriptional mutagenesis
86 auth.
Bert M. Verheijen,
Claire Chung,
Ben Thompson,
Hyunjin Kim,
Asa Nakahara,
J. Anink,
James D. Mills,
H. Phatnani,
Justin Kwan,
D. Sareen,
James R. Broach,
Zachary Simmons,
Ximena Arcila-Londono,
Edward B Lee,
V. V. Van Deerlin,
...
N. Shneider,
Ernest Fraenkel,
L. Ostrow,
F. Baas,
Noah Zaitlen,
James D. Berry,
Andrea Malaspina,
P. Fratta,
Gregory A. Cox,
Leslie M. Thompson,
Steve Finkbeiner,
E. Dardiotis,
Timothy M. Miller,
Siddharthan Chandran,
S. Pal,
E. Hornstein,
D. Macgowan,
T. Heiman-Patterson,
M. G. Hammell,
N. Patsopoulos,
O. Butovsky,
Joshua Dubnau,
Avindra Nath,
Robert Bowser,
Matthew M Harms,
Eleonora Aronica,
Mary Poss,
Jennifer Phillips-Cremins,
John Crary,
N. Atassi,
Dale J. Lange,
Darius J. Adams,
Leonidas Stefanis,
M. Gotkine,
Robert H. Baloh,
Suma Babu,
T. Raj,
S. Paganoni,
Ophir Shalem,
Colin Smith,
Bin Zhang,
Brent Harris,
Iris J. Broce,
V. Drory,
J. Ravits,
C. Mcmillan,
Vilas Menon,
Lani Wu,
Steve Altschuler,
Y. Lerner,
Rita Sattler,
K. Van Keuren-Jensen,
O. Rozenblatt-Rosen,
Kerstin Lindblad-Toh,
Katharine Nicholson,
Peter Gregersen,
J. Lee,
Maze Therapeutics,
Bristol-Myers Squibb,
S. Kõks,
Stephen Muljo,
B. Traynor,
Pfizer,
Regeneron,
Insitro,
J. Lee,
Eleonora Aronica,
Kiyomitsu Oyanagi,
Akiyoshi Kakita,
Jean-Francois Gout,
M. Vermulst
|
3 |
2024 |
3 🐜
|
🐜
|
Safety and activity of anti‐CD14 antibody IC14 (atibuclimab) in ALS: Experience with expanded access protocol
34 auth.
D. Gelevski,
Grace Addy,
M. Rohrer,
Caroline Cohen,
Aimee Roderick,
Allison Winter,
Judith Carey,
J. Scalia,
M. Yerton,
Harli Weber,
Michael Doyle,
Neil Parikh,
Geli Kane,
A. Ellrodt,
Katherine M. Burke,
...
Derek D’Agostino,
E. Sinani,
Hong Yu,
Alexander V. Sherman,
Jan Agosti,
G. Redlich,
Patrick Charmley,
D. Crowe,
Mark Appleby,
Brian Ziegelaar,
Katherine Hanus,
Zhenhua Li,
Suma Babu,
Katharine Nicholson,
Sarah Luppino,
James D Berry,
C. Baecher-Allan,
S. Paganoni,
M. Cudkowicz
|
2 |
2022 |
2 🐜
|
🐜
|
Debamestrocel multimodal effects on biomarker pathways in amyotrophic lateral sclerosis are linked to clinical outcomes
27 auth.
Stacy R Lindborg,
Namita A Goyal,
Jonathan Katz,
Matthew Burford,
Jenny Li,
H. Kaspi,
Natalie Abramov,
Bruno Boulanger,
James D. Berry,
Katharine Nicholson,
T. Mozaffar,
Robert Miller,
Liberty Jenkins,
Robert H. Baloh,
Richard Lewis,
...
N. Staff,
M. Owegi,
Bob Dagher,
Netta R Blondheim-Shraga,
Y. Gothelf,
Y. Levy,
R. Kern,
R. Aricha,
Anthony J Windebank,
Robert Bowser,
Robert H. Brown,
M. Cudkowicz
|
0 |
2024 |
0 🐜
|
🐜
|
Allogeneic B cell immunomodulatory therapy in amyotrophic lateral sclerosis.
26 auth.
R. F. Sîrbulescu,
Katharine Nicholson,
Kento Kawai,
Orla M Hilton,
D. Sobell,
Gina Jin,
David E Verrill,
Liam J Dwyer,
Yueyue Xiong,
Petra Bachanová,
Spencer E Kim,
Shannon Gallup,
Dario Gelevski,
H. Daley,
Diego E Hernandez Rodriguez,
...
H. Negre,
Olive Sturtevant,
S. Nikiforow,
Jerome Ritz,
Yi-Bin Chen,
P. Reeves,
A. Sluder,
James D. Berry,
Ghazaleh Sadri‐Vakili,
M. Cudkowicz,
M. Poznansky
|
0 |
2024 |
0 🐜
|
🐜
|
Immediate postoperative non‐invasive positive pressure ventilation following midface microvascular free flap reconstruction
9 auth.
Andrew R Larson,
Jenny X. Chen,
A. Holman,
Stacey L. Sullivan,
Purris Williams,
Katharine Nicholson,
...
D. Lin,
Yuka Kiyota,
J. Richmon
|
0 |
2021 |
0 🐜
|