🐜
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Risdiplam in Patients Previously Treated with Other Therapies for Spinal Muscular Atrophy: An Interim Analysis from the JEWELFISH Study
207 auth.
C. Chiriboga,
Claudio Bruno,
T. Duong,
Dirk Fischer,
Eugenio Mercuri,
Janbernd Kirschner,
A. Kostera-Pruszczyk,
B. Jaber,
K. Gorni,
H. Kletzl,
I. Carruthers,
Carmen Martín,
Francis Warren,
R. Scalco,
K. Wagner,
...
F. Muntoni,
N. Deconinck,
I. Balikova,
I. Joniau,
V. Tahon,
S. Wittevrongel,
N. Goemans,
C. Cassiman,
L. Prové,
Lisa Vancampenhout,
M. Van den Hauwe,
Annelies Van Impe,
C. Cances,
V. Soler,
Lauriane Maillard De La Morandais,
Delphine Vovan,
P. Cintas,
F. Auriol,
M. Mus,
Gwennaelle Alphonsa,
Valerie Bellio,
Olaia Gil Mato,
F. Flamein,
Cécile Evrard,
Amina Ziouche,
Ikram Bouacha-Allou,
P. Debruyne,
Gilles Derlyn,
S. Defoort,
Florian Leroy,
Loïc Danjoux,
I. Desguerre,
D. Bremond-Gignac,
Maxence Rateuax,
E. Deladrière,
C. Vuillerot,
Quentin Veillerot,
Bénédicte Sibille-Dabadi,
A. Barrière,
M. Tinat,
Manel Saidi,
S. Fontaine,
Camille de Montferrand,
Laure Le-Goff,
Aurélie Portefaix,
U. W. Louvier,
P. Duval,
P. Caradec,
S. Touati,
A. Herranz,
Janbernd Kirschner,
J. Bollig,
Fanni E Molnár,
Sibylle Vogt,
A. Pechmann,
D. Schorling,
S. Wider,
H. Kölbel,
U. Schara,
F. Braun,
A. Gangfuss,
T. Hagenacker,
A. Eckstein,
D. Dekowski,
Michael Oeverhaus,
Mareile Stoehr,
B. Andres,
Karin Smuda,
E. Bertini,
A. D’Amico,
S. Petroni,
P. Valente,
Annamaria Bonetti,
A. Carlesi,
Irene Mizzoni,
Claudio Bruno,
M. Pedemonte,
N. Brolatti,
E. Priolo,
Giuseppe Rao,
Lorenza Sposetti,
S. Morando,
G. Comi,
S. Osnaghi,
Valeria Minorini,
F. Abbati,
F. Fassini,
M. Foà,
M. Lopopolo,
F. Magri,
A. Govoni,
M. Meneri,
V. Parente,
Eugenio Mercuri,
L. Antonaci,
M. Pera,
M. Pane,
G. Amorelli,
Costanza Barresi,
Guglielmo D’Amico,
L. Orazi,
G. Coratti,
R. de Sanctis,
Giuseppe Vita,
M. Sframeli,
G. Vita,
P. Aragona,
Leandro Inferrera,
E. Postorino,
D. Montanini,
Vincenzo Di Bella,
C. Donato,
Elisabetta Calà,
Ludo W. van der Pol,
Jos Aalbers,
J. D. de Boer,
Saskia Imhof,
Pascale Cooijmans,
Thijs Ruyten,
Danny R. van der Woude,
A. Kostera-Pruszczyk,
Beata Klimaszewska,
Dominika Romańczak,
Zuzanna Gierlak-Wójcicka,
Malwina Kępa,
Adam Sikorski,
M. Sobieraj,
A. Lusakowska,
B. Kierdaszuk,
Karolina Czeczko,
Dirk Fischer,
B. Henzi,
K. Gugleta,
Á. Kusnyerik,
P. Siems,
Sabina Akos,
Nora Frei,
Christine Seppi,
Christine Wondrusch Haschke,
M. Guglieri,
V. Straub,
R. Bell,
Mahmoud Nassar,
S. Page,
Michael P. Clarke,
Aedheen Regan,
A. Mayhew,
R. M. Lofra,
D. Parasuraman,
Simone Bruschi,
Abdul-Jabbar Ghauri,
A. Castle,
S. Naqvi,
N. Patt,
M. Scoto,
F. Trucco,
R. Henderson,
R. Kukadia,
W. Moore,
E. Milev,
C. Rye,
V. Selby,
Amy Wolfe,
B. Darras,
Anna Maria Baglieri,
A. Fulton,
Courtney Lucken,
E. Maczek,
A. Pasternak,
C. Chiriboga,
Steven M. Kane,
Ma Edylin M. Bautista,
E. Frommer,
Noelle Pensec,
R. Salazar,
C. Yochai,
Rafael Rodrigues-Torres,
M. Chawla,
J. Day,
Shannon Beres,
R. Gee,
S. Young,
R. Finkel,
A. Nazario,
Airaj F Fasiuddin,
J. Wells,
Jennifer Wilson,
Debbie Berry,
Virgina Rizzo,
Julie M. Duke,
M. Monduy,
J. Collado
|
5 |
2023 |
5 🐜
|
🐜
|
Correction to: Risdiplam in Patients Previously Treated with Other Therapies for Spinal Muscular Atrophy: An Interim Analysis from the JEWELFISH Study
207 auth.
C. Chiriboga,
Claudio Bruno,
T. Duong,
Dirk Fischer,
Eugenio Mercuri,
Janbernd Kirschner,
A. Kostera-Pruszczyk,
B. Jaber,
K. Gorni,
H. Kletzl,
I. Carruthers,
Carmen Martín,
Francis Warren,
R. Scalco,
K. Wagner,
...
Francesco Muntoni,
N. Deconinck,
I. Balikova,
I. Joniau,
V. Tahon,
S. Wittevrongel,
N. Goemans,
C. Cassiman,
L. Prové,
Lisa Vancampenhout,
M. Van den Hauwe,
Annelies Van Impe,
C. Cances,
V. Soler,
Lauriane Maillard De La Morandais,
Delphine Vovan,
P. Cintas,
F. Auriol,
M. Mus,
Gwennaelle Alphonsa,
Valerie Bellio,
Olaia Gil Mato,
F. Flamein,
Cécile Evrard,
Amina Ziouche,
Ikram Bouacha-Allou,
P. Debruyne,
Gilles Derlyn,
S. Defoort,
Florian Leroy,
Loïc Danjoux,
I. Desguerre,
D. Bremond-Gignac,
Maxence Rateuax,
E. Deladrière,
C. Vuillerot,
Quentin Veillerot,
Bénédicte Sibille-Dabadi,
A. Barrière,
M. Tinat,
Manel Saidi,
S. Fontaine,
Camille de Montferrand,
Laure Le-Goff,
Aurélie Portefaix,
U. W. Louvier,
P. Duval,
P. Caradec,
S. Touati,
A. Herranz,
Janbernd Kirschner,
J. Bollig,
Fanni E Molnár,
Sibylle Vogt,
A. Pechmann,
D. Schorling,
S. Wider,
H. Kölbel,
U. Schara,
F. Braun,
A. Gangfuss,
T. Hagenacker,
A. Eckstein,
D. Dekowski,
Michael Oeverhaus,
Mareile Stoehr,
B. Andres,
Karin Smuda,
E. Bertini,
A. D’Amico,
S. Petroni,
P. Valente,
Annamaria Bonetti,
A. Carlesi,
Irene Mizzoni,
Claudio Bruno,
M. Pedemonte,
N. Brolatti,
E. Priolo,
Giuseppe Rao,
Lorenza Sposetti,
S. Morando,
G. Comi,
S. Osnaghi,
Valeria Minorini,
F. Abbati,
F. Fassini,
M. Foà,
M. Lopopolo,
F. Magri,
A. Govoni,
M. Meneri,
V. Parente,
Eugenio Mercuri,
L. Antonaci,
M. Pera,
M. Pane,
G. Amorelli,
Costanza Barresi,
Guglielmo D’Amico,
L. Orazi,
G. Coratti,
R. de Sanctis,
Giuseppe Vita,
M. Sframeli,
G. Vita,
P. Aragona,
Leandro Inferrera,
E. Postorino,
D. Montanini,
Vincenzo Di Bella,
C. Donato,
Elisabetta Calà,
Ludo W. van der Pol,
Jos Aalbers,
J. D. de Boer,
Saskia Imhof,
Pascale Cooijmans,
Thijs Ruyten,
Danny R. van der Woude,
A. Kostera-Pruszczyk,
Beata Klimaszewska,
Dominika Romańczak,
Zuzanna Gierlak-Wójcicka,
Malwina Kępa,
Adam Sikorski,
M. Sobieraj,
A. Lusakowska,
B. Kierdaszuk,
Karolina Czeczko,
Dirk Fischer,
B. Henzi,
K. Gugleta,
Á. Kusnyerik,
P. Siems,
Sabina Akos,
Nora Frei,
Christine Seppi,
Christine Wondrusch Haschke,
M. Guglieri,
V. Straub,
R. Bell,
Mahmoud Nassar,
S. Page,
MichaelP. Clarke,
Aedheen Regan,
A. Mayhew,
R. M. Lofra,
D. Parasuraman,
Simone Bruschi,
Abdul-Jabbar Ghauri,
A. Castle,
S. Naqvi,
N. Patt,
M. Scoto,
F. Trucco,
R. Henderson,
R. Kukadia,
W. Moore,
E. Milev,
C. Rye,
V. Selby,
Amy Wolfe,
B. Darras,
Anna Maria Baglieri,
A. Fulton,
Courtney Lucken,
E. Maczek,
A. Pasternak,
C. Chiriboga,
Steven Kane,
Ma Edylin M. Bautista,
E. Frommer,
Noelle Pensec,
R. Salazar,
C. Yochai,
Rafael Rodrigues-Torres,
M. Chawla,
J. Day,
Shannon Beres,
R. Gee,
S. Young,
R. Finkel,
A. Nazario,
Airaj F Fasiuddin,
J. Wells,
Jennifer B. Wilson,
Debbie Berry,
Virgina Rizzo,
Julie M. Duke,
M. Monduy,
J. Collado
|
0 |
2023 |
0 🐜
|