BetterScholar BetterScholar
3
Role
Title
Level Year L/R
🐜 Safety and efficacy of losmapimod in facioscapulohumeral muscular dystrophy (ReDUX4): a randomised, double-blind, placebo-controlled phase 2b trial
39 auth. R. Tawil, Kathryn Wagner, J. Hamel, Doris Leung, J. Statland, Leo Wang, A. Genge, Sabrina Sacconi, Hanns Lochmüller, David Reyes-Leiva, J. Díaz-Manera, J. Alonso-Pérez, N. Muelas, Juan J. Vílchez, Alan Pestronk, ... S. Gibson, Namita A Goyal, Lawrence Hayward, Nicholas Johnson, S. Lorusso, M. Freimer, Perry B. Shieh, S. Subramony, B. V. Engelen, J. Kools, O. Leinhard, Per Widholm, Christopher Morabito, Christopher Moxham, Diego Cadavid, Michelle Mellion, A. Odueyungbo, W. Tracewell, Anthony Accorsi, L. Ronco, Robert Gould, J. Shoskes, L. A. Rojas, John Jiang
3 2024
3
🐜
🐜 Study Design of AOC 1001-CS1, a Phase 1/2 Clinical Trial Evaluating the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of AOC 1001 Administered Intravenously to Adult Patients with Myotonic Dystrophy Type 1 (DM1) (MARINA) (S23.006)
20 auth. Nicholas Johnson, John Day, J. Hamel, J. Statland, S. Subramony, W. Arnold, Charles Thornton, Matthew Wicklund, P. Soltanzadeh, Ben Knisley, ... Varun Goel, K. Ditrapani, Chao-Yin Chen, Kristi R. Clark, Alissa Peters, C. Heusner, Husam Younis, Mohita Kumar, Li-Jung Tai, E. Ackermann
1 2022
1
🐜
🐜 Frataxin analysis using triple quadrupole mass spectrometry: application to a large heterogeneous clinical cohort.
7 auth. David R Lynch, Teerapat Rojsajjakul, S. Subramony, Susan L. Perlman, Medina Keita, C. Mesaros, ... Ian A Blair
1 2023
1
🐜