Site-Specific Gene Editing of Human Hematopoietic Stem Cells for X-Linked Hyper-IgM Syndrome.
14 auth.
C. Kuo,
Joseph D. Long,
Beatriz Campo-Fernández,
Satiro N De Oliveira,
Aaron R Cooper,
Z. Romero,
Megan D Hoban,
Alok V. Joglekar,
Georgia R Lill,
Michael L Kaufman,
...
S. Fitz-Gibbon,
Xiaoyan Wang,
R. Hollis,
D. Kohn
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6 |
2018 |
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